gene

DNA Gene Therapy Concept

A Potential Cure for Autism: New Research Finds That Gene Therapy Could Treat Pitt-Hopkins Syndrome

A new study has shown that gene therapy may be able to prevent or reverse many deleterious effects of Pitt-Hopkins syndrome New research from the UNC Neuroscience Center lab of Ben Philpot, Ph.D., finds restoring lost gene activity prevents many disease signs in an animal model of Pitt-Hopkins syndrome, a rare, single-gene neurodevelopmental condition. Pitt-Hopkins …

A Potential Cure for Autism: New Research Finds That Gene Therapy Could Treat Pitt-Hopkins Syndrome Read More »

Changing our DNA: 'The age of human therapeutic gene editing is here'

Changing our DNA: ‘The age of human therapeutic gene editing is here’

While Rose spent her short life helping to break down the stigma attached to a devastating illness, geneticist David Liu has dedicated his career to developing ways to alter the genetic code that took her life at such a tender age. “That a single misspelling in her DNA ended Adalia’s life so early is a …

Changing our DNA: ‘The age of human therapeutic gene editing is here’ Read More »